Some genetic disorders—such as cystic fibrosis, hemophilia and Tay Sachs disease—involve many mutations in a person's genome, ...

Explore CRISPR technology explained, gene editing science, DNA modification, and genetic engineering ethics—discover how ...

A new gene-editing technique enables the correction of multiple genetic mutations simultaneously, transforming the prospects ...

In a first for adults in Singapore, scientists are conducting gene editing trials on heart patients to correct defects at ...

We have written about the promise of gene therapy to correct genetic disease many times. An exciting development happened ...

Some of the most expensive drugs currently in use are gene therapies to treat specific diseases, and their high cost limits ...

Investigators at Weill Cornell Medicine have developed a versatile and non-toxic technology for controlling the activity of ...

Complexities like these make it challenging to develop broadly applicable gene therapies for these disorders. Researchers at The University of Texas at Austin now have developed an improved method of ...

Weill Cornell Medicine scientists created Cyclone, a simple tool that uses the antiviral drug acyclovir to safely switch ...

Some gene therapy treatments use modified adeno-associated viruses (AAVs) like the one shown here to deliver therapeutic genetic material into a patient’s cells. In a finding with implications for one ...

This story is part of a series on the current progression in Regenerative Medicine. In 1999, I defined regenerative medicine as the collection of interventions that restore tissues and organs damaged ...