News

This month, 21-year-old Sebastien Beauzile became the first man in New York history to be cured of sickle cell anemia, a genetic blood disorder, thanks to a new form of gene therapy.
The Food and Drug Administration on Friday approved two gene therapies to treat sickle cell disease, one of the which is the first CRISPR/Cas9-based treatment to win regulatory approval in the US.