Zolgensma, which is used to treat spinal muscular atrophy, can cause side effects. Learn about its more common, mild, and serious side effects and how to manage them.

As treatment for spinal muscular atrophy (SMA) has drastically improved over the last decade, so too have survival rates and the number of people with SMA living well into adulthood. | A new ...

Dr Haitham Elbashir, Consultant Pediatric Neurorehabilitation at Al Jalila Children’s Hospital, said, "Zolgensma is a transformative therapy that offers children with SMA the chance to regain strength ...

Shares of Sarepta Therapeutics plunged more than 30% on Friday as the future of its approved gene therapy appeared at risk. Sarepta has reported three patient deaths related to its gene therapies ...

For example, Novartis' gene therapy Zolgensma for spinal muscular atrophy has also caused liver toxicity and death, but the benefit of that treatment is clear.

Kalorama Information, a leading authority in healthcare market research, announces the release of its new report, Cell and Gene Therapy Market Dynamics by Disease Type: Development, Trends, and ...