Zolgensma outperformed Spinraza in achieving a more sustained clinical response for children with SMA type 1, a comparative ...

For columnist Alyssa Silva, control has always been her safety net. But in reality, it doesn't protect her; it exhausts her.

Most children SMA type 1 can survive an episode of pARDS, a life-threatening respiratory failure, under standard protocols, ...

When columnist Connie Chandler tackles an art project, it becomes a creative collaboration thanks to her supportive team of ...

SMA patients may have subtle abnormalities in eye movements, likely caused by changes in the brain rather than muscle ...

A study found mutations that cause SMA may trigger problems with bone cell communication, suggesting a potential new way to treat weak bones.

The change of seasons brings colder weather, meaning columnist Connie Chandler must seek to adapt to her changing physical ...

Columnist Sherry Toh can't fathom generative AI replacing human empathy when it comes to caregiving for people with rare diseases.

Home healthcare requires adaptability, writes columnist Ari Anderson, who has relied on home health nurses for decades.

Columnist Helen Baldwin describes how Halloween lost its mojo for her after her baby boy was diagnosed with SMA in 1997.

Being a wheelchair user has its drawbacks, says columnist Kevin Schaefer, but he's also found many benefits to having a ...