More information: Itsuki Abe et al, Split RNA switch orchestrates pre- and post-translational control to enable cell type-specific gene expression, Nature Communications (2025).

But recent research my colleagues and I conducted has shown that a form of gene therapy can successfully restore hearing in toddlers and young adults born with congenital deafness.

Sea Spiders Lack a Key Body Part and a Missing Gene Could Explain Why Scientists have long sought to understand why sea spiders keep some of their most important organs in their legs.

Changing one gene can restore some tissue regeneration to mice Signaling from retinoic acid appears to be key to getting mice to regrow ear damage.

The FDA has reportedly put the director of its cell and gene therapy office on administrative leave and escorted her out of the agency.

Gene Roddenberry’s son said his father was an atheist. But documented evidence tells a different, more nuanced story about the creator of “Star Trek.” ...

Cutting-edge gene editing technology could eradicate Down syndrome, according to Japanese scientists. Down syndrome, which causes a range of developmental differences and affects 1 in 700 newborns ...

Notably, BPA alone had no effect, but when combined with RA, it caused a dramatic shift in gene expression and brain structure.

Nicole Verdun, top gene therapy regulator at the FDA, has been forced out of the agency.

A second patient has died following treatment with Sarepta Therapeutics’ Elevidys, raising more doubts about the Duchenne muscular dystrophy (DMD) gene therapy’s safety profile. | A second ...

Eli Lilly will acquire gene-editing startup Verve Therapeutics for up to $1.3 billion, the companies said on Tuesday, accelerating a push into experimental cardiovascular therapies.